THERAPEUTIC STRATEGIES FOR THE CORRECTION OF SPLICING IN HEREDITARY DISEASES: METHODS AND CLINICAL TRIALS. Genetics and Molecular Research, [S. l.], 2026. DOI: 10.4238/6nk6ba82. Disponível em: https://geneticsmr.com/index.php/gmr/article/view/1490.. Acesso em: 22 jun. 2026.