GENOME-BASED THERAPEUTIC STRATEGIES TARGETING RARE DISEASES THROUGH PRECISION EDITING AND DELIVERY SYSTEMS. Genetics and Molecular Research, [S. l.], 2026. DOI: 10.4238/5bx3nx71. Disponível em: https://geneticsmr.com/index.php/gmr/article/view/650.. Acesso em: 17 may. 2026.